PROTÓTIPO
Discussão de Artigos
Aqui encontrará resumos estruturados de ensaios clínicos de fase II e III publicados em revistas indexadas. O intúito desta seção é a dissecação dos dados de eficácia, segurança e desenho de estudo.

Lifileucel, a Tumor-Infiltrating Lymphocyte
Therapy, in Metastatic Melanoma

Exagamglogene Autotemcel for Transfusion-Dependent β-Thalassemia

CRISPR-Cas9 In Vivo Gene Editing for Hereditary Angioedema

Ciltacabtagene Autoleucel or Standard Care in Lenalidomide-Refractory Multiple Myeloma (CARTITUDE-4)

Ide-cel or Standard Regimens in Relapsed and Refractory Multiple Myeloma (KarMMa-3)

Valoctocogene Roxaparvovec Gene Therapy for Severe Hemophilia A (GENEr8-1)
Terapias Emergentes

Delandistrogene Moxeparvovec for Duchenne Muscular Dystrophy

Lifileucel, a Tumor-Infiltrating Lymphocyte Therapy, in Metastatic Melanoma

Exagamglogene Autotemcel for Severe Sickle Cell Disease

Immunotherapy Using Tumor Infiltrating Lymphocytes for Patients With Metastatic Cancer

Trends in mesenchymal stem cell-derived extracellular vesicles clinical trials 2014–2024: is efficacy optimal in a narrow dose range?

Exagamglogene Autotemcel for Severe Sickle Cell Disease
